Seven-year follow-up of durability and safety of AAV CNS gene therapy for a lysosomal storage disorder in a large animal
Xavier Sánchez, Yvonne Espada, Carles Roca, Víctor Sánchez, Xavier León, Anna Andaluz, Joan Bertolin, Jennifer Pérez, Albert Ribera, Sonia Añor, Ana Carretero, Gemma Elias, Maria Luisa Jaén, Martí Pumarola, Sara Marcó, Maria Molas, Virginia Haurigot, Miguel Garcia, Fatima Bosch*, Marc Navarro
Profundice en los temas de investigación de 'Seven-year follow-up of durability and safety of AAV CNS gene therapy for a lysosomal storage disorder in a large animal'. En conjunto forman una huella única.