Long-Term Phenotypic Correction of Fanconi Anemia-A Patients Treated by Gene Therapy in Early Stages of the Bone Marrow Failure

Paula Rio; Julian Sevilla; Susana Navarro; Josune Zubicaray; Rebeca Sanchez-Dominguez; Eileen Nicoletti; Wei Wang; Roser M. Pujol; Michael Rothe; Jose C. Segovia; Rosa M. Yanez; Jose A. Casado; Yari Gimenez; Omaira Alberquilla; Elena Almarza; Jordi Barquinero; Nagore Garcia de Andoin; Ricardo Lopez; Albert Catala; Francois Lefrere; Marina Cavazzana; Manfred Schmidt; Axel Schambach; Gayatri Rao; Jordi Surralles; Jean Soulier; Cristina Diaz de Heredia; Jonathan D. Schwartz; Juan A. Bueren

doi:10.1016/j.ymthe.2022.04.017

Long-Term Phenotypic Correction of Fanconi Anemia-A Patients Treated by Gene Therapy in Early Stages of the Bone Marrow Failure

Paula Rio, Julian Sevilla, Susana Navarro, Josune Zubicaray, Rebeca Sanchez-Dominguez, Eileen Nicoletti, Wei Wang, Roser M. Pujol, Michael Rothe, Jose C. Segovia, Rosa M. Yanez, Jose A. Casado, Yari Gimenez, Omaira Alberquilla, Elena Almarza, Jordi Barquinero, Nagore Garcia de Andoin, Ricardo Lopez, Albert Catala, Francois LefrereMarina Cavazzana, Manfred Schmidt, Axel Schambach, Gayatri Rao, Jordi Surralles, Jean Soulier, Cristina Diaz de Heredia, Jonathan D. Schwartz, Juan A. Bueren

Departamento de Genética y Microbiología

Producción científica: Contribución a una revista › Artículo › Investigación › revisión exhaustiva

1 Citas (Web of Science)

Idioma original	Inglés
Páginas (desde-hasta)	370-370
Número de páginas	1
Publicación	Molecular Therapy
Volumen	30
N.º	4
DOI	https://doi.org/10.1016/j.ymthe.2022.04.017
Estado	Publicada - abr 2022

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10.1016/j.ymthe.2022.04.017

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Rio, P., Sevilla, J., Navarro, S., Zubicaray, J., Sanchez-Dominguez, R., Nicoletti, E., Wang, W., Pujol, R. M., Rothe, M., Segovia, J. C., Yanez, R. M., Casado, J. A., Gimenez, Y., Alberquilla, O., Almarza, E., Barquinero, J., de Andoin, N. G., Lopez, R., Catala, A., ... Bueren, J. A. (2022). Long-Term Phenotypic Correction of Fanconi Anemia-A Patients Treated by Gene Therapy in Early Stages of the Bone Marrow Failure. Molecular Therapy, 30(4), 370-370. https://doi.org/10.1016/j.ymthe.2022.04.017

@article{4ff8f04bc7eb43deb8aa24e4bf091bcc,

title = "Long-Term Phenotypic Correction of Fanconi Anemia-A Patients Treated by Gene Therapy in Early Stages of the Bone Marrow Failure",

author = "Paula Rio and Julian Sevilla and Susana Navarro and Josune Zubicaray and Rebeca Sanchez-Dominguez and Eileen Nicoletti and Wei Wang and Pujol, {Roser M.} and Michael Rothe and Segovia, {Jose C.} and Yanez, {Rosa M.} and Casado, {Jose A.} and Yari Gimenez and Omaira Alberquilla and Elena Almarza and Jordi Barquinero and {de Andoin}, {Nagore Garcia} and Ricardo Lopez and Albert Catala and Francois Lefrere and Marina Cavazzana and Manfred Schmidt and Axel Schambach and Gayatri Rao and Jordi Surralles and Jean Soulier and {de Heredia}, {Cristina Diaz} and Schwartz, {Jonathan D.} and Bueren, {Juan A.}",

year = "2022",

month = apr,

doi = "10.1016/j.ymthe.2022.04.017",

language = "English",

volume = "30",

pages = "370--370",

journal = "Molecular Therapy",

issn = "1525-0016",

number = "4",

}

Rio, P, Sevilla, J, Navarro, S, Zubicaray, J, Sanchez-Dominguez, R, Nicoletti, E, Wang, W, Pujol, RM, Rothe, M, Segovia, JC, Yanez, RM, Casado, JA, Gimenez, Y, Alberquilla, O, Almarza, E, Barquinero, J, de Andoin, NG, Lopez, R, Catala, A, Lefrere, F, Cavazzana, M, Schmidt, M, Schambach, A, Rao, G, Surralles, J, Soulier, J, de Heredia, CD, Schwartz, JD & Bueren, JA 2022, 'Long-Term Phenotypic Correction of Fanconi Anemia-A Patients Treated by Gene Therapy in Early Stages of the Bone Marrow Failure', Molecular Therapy, vol. 30, n.º 4, pp. 370-370. https://doi.org/10.1016/j.ymthe.2022.04.017

TY - JOUR

T1 - Long-Term Phenotypic Correction of Fanconi Anemia-A Patients Treated by Gene Therapy in Early Stages of the Bone Marrow Failure

AU - Rio, Paula

AU - Sevilla, Julian

AU - Navarro, Susana

AU - Zubicaray, Josune

AU - Sanchez-Dominguez, Rebeca

AU - Nicoletti, Eileen

AU - Wang, Wei

AU - Pujol, Roser M.

AU - Rothe, Michael

AU - Segovia, Jose C.

AU - Yanez, Rosa M.

AU - Casado, Jose A.

AU - Gimenez, Yari

AU - Alberquilla, Omaira

AU - Almarza, Elena

AU - Barquinero, Jordi

AU - de Andoin, Nagore Garcia

AU - Lopez, Ricardo

AU - Catala, Albert

AU - Lefrere, Francois

AU - Cavazzana, Marina

AU - Schmidt, Manfred

AU - Schambach, Axel

AU - Rao, Gayatri

AU - Surralles, Jordi

AU - Soulier, Jean

AU - de Heredia, Cristina Diaz

AU - Schwartz, Jonathan D.

AU - Bueren, Juan A.

PY - 2022/4

Y1 - 2022/4

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U2 - 10.1016/j.ymthe.2022.04.017

DO - 10.1016/j.ymthe.2022.04.017

M3 - Article

SN - 1525-0016

VL - 30

SP - 370

EP - 370

JO - Molecular Therapy

JF - Molecular Therapy

IS - 4

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