Specific Expression of Glial-Derived Neurotrophic Factor in Muscles as Gene Therapy Strategy for Amyotrophic Lateral Sclerosis

Guillem Mòdol-Caballero, Belén García-Lareu, Mireia Herrando-Grabulosa, Sergi Verdés, Rubén López-Vales, Gemma Pagès, Miguel Chillón, Xavier Navarro, Assumpció Bosch

Research output: Contribution to journalArticleResearchpeer-review

4 Citations (Scopus)
1 Downloads (Pure)
Original languageEnglish
Number of pages14
JournalNeurotherapeutics
Volume18
Issue number2
DOIs
Publication statusPublished - 30 Mar 2021

Keywords

  • AAV
  • Amyotrophic lateral sclerosis
  • GDNF
  • Gene therapy
  • Motoneuron
  • Neuromuscular junction

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