Long-term and significant correction of brain lesions in adult mucopolysaccharidosis type VII mice using recombinant AAV vectors

A. Bosch, E. Perret, N. Desmaris, J.M. Heard

Research output: Contribution to journalArticleResearch

115 Citations (Scopus)
Original languageEnglish
Pages (from-to)63-70
JournalMolecular therapy (Print)
Volume1
Issue number1
Publication statusPublished - 1 Jan 2000

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