Keyphrases
Liver
100%
Mucopolysaccharidosis Type IIIA
100%
CNS Pathologies
100%
Sulfamidase
100%
Gene Transfer
60%
Glycosaminoglycans
60%
Liver-directed
60%
Therapeutic Benefits
40%
Genetic Modification
20%
Lysosomal Storage Disease
20%
Cerebellum
20%
Skeletal muscle
20%
Adeno-associated Viral Vector
20%
Neuropathology
20%
Heparan Sulfate
20%
Adenovirus
20%
Plasma Parameters
20%
Cortex
20%
Progressive Neurodegeneration
20%
AAV8
20%
American Society
20%
Disease Phenotype
20%
Intramuscular Administration
20%
Somatic Alterations
20%
Somatic Tissues
20%
Gene-cell Therapy
20%
Supraphysiological
20%
Medicine and Dentistry
Mucopolysaccharidosis
100%
N Sulfoglucosamine Sulfohydrolase
100%
Gene Transfer
60%
Somatics
60%
Glycosaminoglycan
60%
Diseases
20%
Gene Therapy
20%
Cell Therapy
20%
Neurodegeneration
20%
Adeno Associated Virus Vector
20%
Adeno-Associated Virus
20%
Lifespan
20%
Intramuscular Injection
20%
Heparan Sulfate
20%
Lysosomal Storage Disease
20%
Cerebellum
20%
Neurological Pathology
20%
Skeletal Muscle
20%
Neuroscience
N Sulfoglucosamine Sulfohydrolase
100%
Gene Delivery
75%
Somatics
75%
Gene Transfer
75%
Glycosaminoglycan
75%
Cerebellum
25%
Neurodegeneration
25%
Heparan Sulfate
25%
Cell Therapy
25%
Adeno Associated Virus Vector
25%
Adeno-Associated Virus
25%
Skeletal Muscle
25%
Blood Plasma
25%
Pharmacology, Toxicology and Pharmaceutical Science
Mucopolysaccharidosis
100%
N Sulfoglucosamine Sulfohydrolase
100%
Glycosaminoglycan
60%
Gene Delivery
60%
Adeno Associated Virus
20%
Disease
20%
Lysosome Storage Disease
20%
Nerve Degeneration
20%
Adeno Associated Virus Vector
20%
Heparan Sulfate
20%
Intramuscular Injection
20%
Biochemistry, Genetics and Molecular Biology
Mucopolysaccharidosis
100%
Glycosaminoglycan
60%
Lysosomal Storage Disease
20%
Enzyme
20%
Skeletal Muscle
20%
Adeno Associated Virus Vector
20%
Blood Level
20%
Lifespan
20%
DNA Modification
20%
Adeno Associated Virus
20%
Heparan Sulfate
20%