Full correction of neurologic and somatic lysosomal pathology in Mucopolysaccharidosis type IIIB by AAV9-based gene therapy

V Haurigot; A Ribera; S Marco; M Garcia; S Motas; P Villacampa; V Sanchez; L Maggioni; C Roca; X Leon; M Molas; null Munoz S; J Ruberte; F Mingozzi; X Moll; S Anor; F. Bosch

Full correction of neurologic and somatic lysosomal pathology in Mucopolysaccharidosis type IIIB by AAV9-based gene therapy

V Haurigot, A Ribera, S Marco, M Garcia, S Motas, P Villacampa, V Sanchez, L Maggioni, C Roca, X Leon, M Molas, Munoz S, J Ruberte, F Mingozzi, X Moll, S Anor, F. Bosch

Research output: Contribution to journal › Article › Research

Original language	English
Pages (from-to)	A37-
Journal	Human Gene Therapy
Volume	25
Issue number	11
Publication status	Published - 1 Jan 2014

Cite this

Haurigot, V ; Ribera, A ; Marco, S ; Garcia, M ; Motas, S ; Villacampa, P ; Sanchez, V ; Maggioni, L ; Roca, C ; Leon, X ; Molas, M ; Munoz S, ; Ruberte, J ; Mingozzi, F ; Moll, X ; Anor, S ; Bosch, F. / Full correction of neurologic and somatic lysosomal pathology in Mucopolysaccharidosis type IIIB by AAV9-based gene therapy. In: Human Gene Therapy. 2014 ; Vol. 25, No. 11. pp. A37-.

@article{d3bf6c04f8a849bc814173e9d16ab809,

title = "Full correction of neurologic and somatic lysosomal pathology in Mucopolysaccharidosis type IIIB by AAV9-based gene therapy",

author = "V Haurigot and A Ribera and S Marco and M Garcia and S Motas and P Villacampa and V Sanchez and L Maggioni and C Roca and X Leon and M Molas and {Munoz S} and J Ruberte and F Mingozzi and X Moll and S Anor and F. Bosch",

year = "2014",

month = jan,

day = "1",

language = "English",

volume = "25",

pages = "A37--",

journal = "Human Gene Therapy",

issn = "1043-0342",

publisher = "Mary Ann Liebert Inc.",

number = "11",

}

Full correction of neurologic and somatic lysosomal pathology in Mucopolysaccharidosis type IIIB by AAV9-based gene therapy. / Haurigot, V; Ribera, A; Marco, S; Garcia, M; Motas, S; Villacampa, P; Sanchez, V; Maggioni, L; Roca, C; Leon, X; Molas, M; Munoz S, ; Ruberte, J; Mingozzi, F; Moll, X ; Anor, S ; Bosch, F.

In: Human Gene Therapy, Vol. 25, No. 11, 01.01.2014, p. A37-.

Research output: Contribution to journal › Article › Research

TY - JOUR

T1 - Full correction of neurologic and somatic lysosomal pathology in Mucopolysaccharidosis type IIIB by AAV9-based gene therapy

AU - Haurigot, V

AU - Ribera, A

AU - Marco, S

AU - Garcia, M

AU - Motas, S

AU - Villacampa, P

AU - Sanchez, V

AU - Maggioni, L

AU - Roca, C

AU - Leon, X

AU - Molas, M

AU - Munoz S, null

AU - Ruberte, J

AU - Mingozzi, F

AU - Moll, X

AU - Anor, S

AU - Bosch, F.

PY - 2014/1/1

Y1 - 2014/1/1

M3 - Article

VL - 25

SP - A37-

JO - Human Gene Therapy

JF - Human Gene Therapy

SN - 1043-0342

IS - 11

ER -