Follow-Up of a Phase I/II Gene Therapy Trial in Patients with Fanconi Anemia, Subtype A

Julian Sevilla, Paula Rio, Susana Navarro, Rebeca Sanchez-Dominguez, Jose C. Segovia, Wei Wang, Josune Zubicaray, Rosa Yanez, Jose A. Casado, Yari Gimenez, Francisco J. Roman-Rodriguez, Omaira Alberquilla, Eva Galvez, Eva Merino, Jordi Barquinero, Anne Galy, Nagore Garcia de Andoin, Ricardo Lopez, Albert Catala, Francois LefrereMarina Cavazzana, Gayatri Rao, Jonathan Schwartz, Roser M. Pujol, Jordi Surralles, Jean Soulier, Manfred Schmidt, Cristina Diaz de Heredia, Juan Bueren

Research output: Contribution to journalArticleResearchpeer-review

1 Citation (Web of Science)
Original languageEnglish
Pages (from-to)18-18
Number of pages1
JournalMolecular Therapy
Volume29
Issue number4
Publication statusPublished - 27 Apr 2021

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