Evidence supporting regulatory-decision making on orphan medicinal products authorisation in Europe: methodological uncertainties

Caridad Pontes, Juan Manuel Fontanet, Roser Vives, Aranzazu Sancho, Mònica Gómez-Valent, José Ríos, Rosa Morros, Jorge Martinalbo, Martin Posch, Armin Koch, Kit Roes, Katrien Oude Rengerink, Josep Torrent-Farnell, Ferran Torres

Department of Pharmacology, Therapeutics and Toxicology

Research output: Contribution to journal › Article › Research › peer-review

40 Citations (Scopus)

3 results
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Estudi de caracterització del disseny d’assajos clínics realitzats amb medicaments orfes.
Fontanet Sacristan, J. M. (Author), Torrent Farnell, J. (Director) & Pontes García, C. (Director), 14 Sept 2017
Student thesis: Doctoral thesis
Proposal for a new classification of orphan and/or rare conditions based on clinical characteristics that determine the applicability of different research methods to their study
Gomez Valent, M. (Author), Pontes Garcia, C. (Director), 7 Jul 2017
Student thesis: Doctoral thesis
New clinical trial designs applied to the study of orphan and rare diseases: feasibility of methodological guidance to clinical development of new treatments from a regulatory perspective
Sancho López, A. (Author), Pontes Garcia, C. (Director) & Torres, F. (Director), 23 Nov 2018
Student thesis: Doctoral thesis