Biochemical, histological and functional correction of mucopolysaccharidosis Type IIIB by intra-cerebrospinal fluid gene therapy

Virginia Haurigot Mendonça, Miguel Garcia, Xavier Moll Sánchez, Martí Pumarola i Batlle, Jesús Ruberte, Sònia Añor Torres, Fàtima Bosch i Tubert, Albert Ribera Sánchez, Sara Marcó, Sandra Motas, Pilar Villacampa Alcubierre, Luca Maggioni, Xavier León, María Molas, Víctor Sánchez, Sergio Muñoz, Christian Leborgne, Federico Mingozzi

Généthon. Centre de Recherche et d'applications sur les thérapies géniques

Research output: Contribution to journal › Article › Research › peer-review

48 Citations (Scopus)

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Ingenieria Genetica del Musculo Esqueletico para Expresar Insulina y/o Glucoquinasa para el Tratamineto de la Diabetes Mellitus
Bosch Tubert, M. F. (Principal Investigator), Ayuso López, E. (Investigator), Callejas Castiñeiras, D. (Investigator), Casellas Comallonga, A. (Investigator), Elias Puigdomenech, I. (Investigator), Haurigot Mendoça, V. (Investigator), Jimenez, V. (Investigator), Lage Fernandez, R. (Investigator), León Madrenas, X. (Investigator), Maggioni , L. (Investigator), Mallol Dominguez, C. (Investigator), Molas Laplana, M. (Investigator), Morro Larrubia, M. (Investigator), Otaegui Goya, P. J. (Investigator), Ribera Sanchez, A. (Investigator), Vila Prats, L. (Investigator) & Villacampa Alcubierre, P. (Investigator)
Spanish Ministry of Science and Innovation
1/01/12 → 31/12/14
Project: Research Projects and Other Grants